Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 04:34:06 GMT 2025
by
admin
on
Wed Apr 02 04:34:06 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependovirus |
| Organism Species | adeno-associated virus |
| Infraspecific Type | SUBSTRAIN |
| Infraspecific Name | adeno-associated virus type 2/6 (rAAV Rep2-Cap6) vector, which contains a promoterless human coagulation factor IX (hF9, Factor IX or FIX) transgene cassette |
| Part | whole |
| Record UNII |
J177M7U2XK
|
| Record Status |
Validated (UNII)
|
| Record Version |
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-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
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Official Name | English | ||
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Preferred Name | English | ||
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Common Name | English | ||
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Systematic Name | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
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10978
Created by
admin on Wed Apr 02 04:34:06 GMT 2025 , Edited by admin on Wed Apr 02 04:34:06 GMT 2025
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PRIMARY | |||
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2143579-02-4
Created by
admin on Wed Apr 02 04:34:06 GMT 2025 , Edited by admin on Wed Apr 02 04:34:06 GMT 2025
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PRIMARY | |||
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C171790
Created by
admin on Wed Apr 02 04:34:06 GMT 2025 , Edited by admin on Wed Apr 02 04:34:06 GMT 2025
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PRIMARY | |||
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100000177773
Created by
admin on Wed Apr 02 04:34:06 GMT 2025 , Edited by admin on Wed Apr 02 04:34:06 GMT 2025
|
PRIMARY | |||
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J177M7U2XK
Created by
admin on Wed Apr 02 04:34:06 GMT 2025 , Edited by admin on Wed Apr 02 04:34:06 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
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INNOVATOR->PARENT |
| Related Record | Type | Details | ||
|---|---|---|---|---|
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ACTIVE MOIETY |
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| TRANSGENE | ADLINACOGENE CIVAPARVOVEC TRANSGENE INSERT | UM90H33QOQ |