U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 06:15:09 GMT 2025
Edited
by admin
on Wed Apr 02 06:15:09 GMT 2025
Nucleic Acid Type VECTOR
Sequence Origin HUMAN/VIRAL
Sequence Type COMPLETE
Record UNII
UM90H33QOQ
Record Status FAILED
Record Version
  • Download
Name Type Language
ADLINACOGENE CIVAPARVOVEC TRANSGENE INSERT
Common Name English
PROMOTERLESS HUMAN COAGULATION FACTOR IX (HF9, FACTOR IX OR FIX) TRANSGENE CASSETTE, ENCODING EXONS 2-8 AND SPLICE ACCEPTOR SITE SEQUENCE (SA) FROM HF9 EXON 2, FLANKED BY A SEQUENCE HOMOLOGOUS TO THE ZINC-FINGER NUCLEASE (ZFN) CLEAVAGE SITE OF THE HUMAN
Preferred Name English
Code System Code Type Description
FDA UNII
UM90H33QOQ
Created by admin on Wed Apr 02 06:15:09 GMT 2025 , Edited by admin on Wed Apr 02 06:15:09 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_2474 2474 / 2474
Linkage Site Range Site Count
Phosphate 1_1-1_2474 2474 / 2473