U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Tue Apr 01 22:36:01 GMT 2025
Edited
by admin
on Tue Apr 01 22:36:01 GMT 2025
Source Materials Class ORGANISM
Source Materials Type HUMAN
Source Materials State LIVE
Source Materials Parent
Development Stage NEONATAL
Part Location UMBILICAL CORD
Part blood
Fraction Name cd34+ hspc fraction
Record UNII
DBD2HM3I4V
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Dorocubicel
INN   USAN  
Official Name English
ALLOGENEIC HUMAN UMBILICAL CORD BLOOD EXPANDED WITH UM-171
Preferred Name English
dorocubicel [INN]
Common Name English
Allogeneic human umbilical cord blood derived CD34+ hematopoietic stem and progenitor cells (HSPCs). The CD34+ HSPC fraction is selected from cord blood and expanded ex vivo in serum-free growth medium in the presence of UM171 (trans-N1 -[2-benzyl-7-(2-m
Common Name English
CORD BLOOD EXPANDED WITH UM-171
Common Name English
DOROCUBICEL [USAN]
Common Name English
Haematopoietic stem cells and blood progenitors umbilical cord-derived expanded with UM171 ((1R, 4R)-N1-(2-benzyl-7-(2-methyl-2H-tetrazol-5-yl)-9H-pyrimido[4,5-b]indol-4-yl)cyclohexane-1,4-diamine dihydrobromide). The reagent used for MN-172 is known in
Common Name English
ECT-001-CB
Code English
Classification Tree Code System Code
WHO-ATC B05AX04
Created by admin on Tue Apr 01 22:36:01 GMT 2025 , Edited by admin on Tue Apr 01 22:36:01 GMT 2025
FDA ORPHAN DRUG 661418
Created by admin on Tue Apr 01 22:36:01 GMT 2025 , Edited by admin on Tue Apr 01 22:36:01 GMT 2025
Code System Code Type Description
INN
12158
Created by admin on Tue Apr 01 22:36:01 GMT 2025 , Edited by admin on Tue Apr 01 22:36:01 GMT 2025
PRIMARY
USAN
MN-172
Created by admin on Tue Apr 01 22:36:01 GMT 2025 , Edited by admin on Tue Apr 01 22:36:01 GMT 2025
PRIMARY
NCI_THESAURUS
C203130
Created by admin on Tue Apr 01 22:36:01 GMT 2025 , Edited by admin on Tue Apr 01 22:36:01 GMT 2025
PRIMARY
SMS_ID
300000010242
Created by admin on Tue Apr 01 22:36:01 GMT 2025 , Edited by admin on Tue Apr 01 22:36:01 GMT 2025
PRIMARY
FDA UNII
DBD2HM3I4V
Created by admin on Tue Apr 01 22:36:01 GMT 2025 , Edited by admin on Tue Apr 01 22:36:01 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY
stem cell transplantation

Agent Modifications

Modification Process Modification Role Modification Type Amount Fragment Name Fragment ID
CULTURE EXPANSION BIOLOGICAL HUMAN INTERLEUKIN-6 4O4QWG0B3C
CULTURE ACTIVATOR BIOLOGICAL UM-171 DIHYDROBROMIDE DIHYDRATE 9VB5UBJ45H
CULTURE EXPANSION BIOLOGICAL THROMBOPOIETIN 5651J3R2JF
CULTURE EXPANSION BIOLOGICAL HUMAN SOLUBLE KIT LIGAND ED35EH7CP2
Name Property Type Amount Referenced Substance Defining Parameters References
ANTIGEN EXPRESSED BIOLOGICAL