Cyclic pyranopterin monophosphate is a precursor to molybdenum cofactor, which is required for the enzyme activity of sulfite oxidase, xanthine dehydrogenase/oxidase, and aldehyde oxidase. The drug is being investigated in severe molybdenum cofactor deficiency type A. In a clinical study, intravenous administration of the drug resulted in greatly improved neurodevelopmental outcome when started sufficiently early.
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Concept
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X41B5W735T
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Validated (UNII)
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C174941
Created by
admin on Sat Jun 26 12:49:05 UTC 2021 , Edited by admin on Sat Jun 26 12:49:05 UTC 2021
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2301083-34-9
Created by
admin on Sat Jun 26 12:49:05 UTC 2021 , Edited by admin on Sat Jun 26 12:49:05 UTC 2021
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145722612
Created by
admin on Sat Jun 26 12:49:05 UTC 2021 , Edited by admin on Sat Jun 26 12:49:05 UTC 2021
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SUB197141
Created by
admin on Sat Jun 26 12:49:05 UTC 2021 , Edited by admin on Sat Jun 26 12:49:05 UTC 2021
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X41B5W735T
Created by
admin on Sat Jun 26 12:49:05 UTC 2021 , Edited by admin on Sat Jun 26 12:49:05 UTC 2021
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PRIMARY |
This is a non-substance concept
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PARENT -> SALT/SOLVATE |
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ACTIVE MOIETY |
This is a non-substance concept