Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 12:18:05 GMT 2025
by
admin
on
Wed Apr 02 12:18:05 GMT 2025
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| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependoparvovirus |
| Organism Species | adeno-associated dependoparvovirus b |
| Infraspecific Type | RECOMBINANT VECTOR |
| Infraspecific Name | rAAV3B-ATP7Bmini (AAV2LTR/AAV3Bcapsid-ATP7Bmini) |
| Part | whole |
| Record UNII |
C4J4L5V7XS
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| Record Status |
Validated (UNII)
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| Record Version |
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-
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Preferred Name | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Common Name | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
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2773545-20-1
Created by
admin on Wed Apr 02 12:18:05 GMT 2025 , Edited by admin on Wed Apr 02 12:18:05 GMT 2025
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PRIMARY | |||
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C203112
Created by
admin on Wed Apr 02 12:18:05 GMT 2025 , Edited by admin on Wed Apr 02 12:18:05 GMT 2025
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PRIMARY | |||
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300000019591
Created by
admin on Wed Apr 02 12:18:05 GMT 2025 , Edited by admin on Wed Apr 02 12:18:05 GMT 2025
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PRIMARY | |||
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C4J4L5V7XS
Created by
admin on Wed Apr 02 12:18:05 GMT 2025 , Edited by admin on Wed Apr 02 12:18:05 GMT 2025
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PRIMARY | |||
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12798
Created by
admin on Wed Apr 02 12:18:05 GMT 2025 , Edited by admin on Wed Apr 02 12:18:05 GMT 2025
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PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
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ACTIVE MOIETY |
Preclinical; The biological activity of VTX-801 allows restoring defective ATP7B function
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Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| INSERTED GENE EXPRESSION VECTOR | Nimatpagene pariparvovec transgene insert | LLR6QA66HW | ||||
| VIRAL CAPSID | UNSPECIFIED SUBSTANCE |
65f6429a
(not in database)
|
||||
| VIRAL CAPSID | UNSPECIFIED SUBSTANCE |
a84a61b9
(not in database)
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| VIRAL CAPSID | UNSPECIFIED SUBSTANCE |
72b059a1
(not in database)
|