U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 11:22:38 GMT 2025
Edited
by admin
on Wed Apr 02 11:22:38 GMT 2025
Nucleic Acid Type VECTOR
Sequence Origin VIRAL
Sequence Type COMPLETE
Record UNII
LLR6QA66HW
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Nimatpagene pariparvovec transgene insert
Preferred Name English
Code System Code Type Description
FDA UNII
LLR6QA66HW
Created by admin on Wed Apr 02 11:22:38 GMT 2025 , Edited by admin on Wed Apr 02 11:22:38 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_3807 3807 / 3807
Linkage Site Range Site Count
Phosphate 1_2-1_3807 3806 / 3806
Name Property Type Amount Referenced Substance Defining Parameters References
ATP7B-minigene NUCLEIC ACID FEATURE
LIVER-SPECIFIC HUMAN ALPHA-1 ANTITRYPSIN (AAT) PROMOTER NUCLEIC ACID FEATURE
3'-LTR NUCLEIC ACID FEATURE
Poly A NUCLEIC ACID FEATURE
5'-LTR NUCLEIC ACID FEATURE