Zertomibgene Cazparvovec

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Wed Apr 02 21:25:57 GMT 2025` Edited by `admin` on `Wed Apr 02 21:25:57 GMT 2025`
Source Materials Class	ORGANISM
Source Materials Type	RECOMBINANT VIRUS
Organism Family	Parvoviridae
Organism Genus	Dependoparvovirus
Organism Species	adeno-associated dependoparvovirus a
Infraspecific Type	RECOMBINANT VECTOR
Infraspecific Name	TN-201(pCard1/wild-type MYBPC3)
Part	whole
Record UNII	64SQ6WC9ET
Record Status	`Validated (UNII)`
Record Version

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Name

Type

Language

Zertomibgene Cazparvovec

Official Name

English

DNA (recombinant replication-deficient adeno-associated virus 9 vector TN-201 synthetic cardiac-selective promoter plus human myosin-binding protein MYBPC3 transgene plus synthetic polyadenylation signal plus adeno-associated virus 2 inverted terminal re

Preferred Name

English

zertomibgene cazparvovec [INN]

Common Name

English

recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector, encoding myosin-binding protein C (MYBPC3), under control of a synthetic cardiomyocyte-specific cardiac troponin T2 (TNNT2) promoter (pCard1) and a synthetic polyadenylation s

Common Name

English

Code System Code Type Description

SMS_ID

300000038205