U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 19:51:06 GMT 2025
Edited
by admin
on Wed Apr 02 19:51:06 GMT 2025
Nucleic Acid Type VECTOR
Sequence Origin VIRAL, HUMAN
Sequence Type COMPLETE
Record UNII
PLG7E7Y4CW
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Zertomibgene cazparvovec transgene insert
Preferred Name English
Code System Code Type Description
FDA UNII
PLG7E7Y4CW
Created by admin on Wed Apr 02 19:51:06 GMT 2025 , Edited by admin on Wed Apr 02 19:51:06 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_4713 4713 / 4713
Linkage Site Range Site Count
Phosphate 1_2-1_4713 4712 / 4712
Name Property Type Amount Referenced Substance Defining Parameters References
MYBPC3 NUCLEIC ACID FEATURE
ITRs NUCLEIC ACID FEATURE