U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
Evazarsen
INN   USAN  
Official Name English
DNA, D(P-THIO)((2'-O-(2-METHOXYETHYL))M5RC-(2'-O-(2-METHOXYETHYL))RA-(2'-O-(2-METHOXYETHYL))M5RC-(2'-O-(2-METHOXYETHYL))RA-(2'-O-(2-METHOXYETHYL))RA-A-M5C-A-A-G-M5C-T-G-G-T-(2'-O-(2-METHOXYETHYL))M5RC-(2'-O-(2-METHOXYETHYL))RG-(2'-O-(2-METHOXYETHYL))RG-(
Systematic Name English
ISIS-757456
Code English
ISIS-654472 5'-GALNAC CONJUGATE
Code English
evazarsen [INN]
Common Name English
ALL-P-AMBO-5'-O-(((6-(5-((TRIS(3-(6-(2-ACETAMIDO-2-DEOXY-.BETA.-D-GALACTOPYRANOSYLOXY)HEXYLAMINO)-3-OXOPROPOXYMETHYL))METHYL)AMINO-5-OXOPENTANAMIDO)HEXYL))PHOSPHO)-2'-O-(2-METHOXYETHYL)-5-METHYL-P-THIOCYTIDYLYL-(3'-O->5'-O)-2'-O-(2-METHOXYETHYL)-P-THIOAD
Systematic Name English
EVAZARSEN [USAN]
Common Name English
Code System Code Type Description
FDA UNII
P048YHG804
Created by admin on Sat Dec 16 14:18:06 UTC 2023 , Edited by admin on Sat Dec 16 14:18:06 UTC 2023
PRIMARY
INN
12355
Created by admin on Sat Dec 16 14:18:06 UTC 2023 , Edited by admin on Sat Dec 16 14:18:06 UTC 2023
PRIMARY
USAN
JK-205
Created by admin on Sat Dec 16 14:18:06 UTC 2023 , Edited by admin on Sat Dec 16 14:18:06 UTC 2023
PRIMARY
CAS
2589926-22-5
Created by admin on Sat Dec 16 14:18:06 UTC 2023 , Edited by admin on Sat Dec 16 14:18:06 UTC 2023
PRIMARY
NCI_THESAURUS
C188610
Created by admin on Sat Dec 16 14:18:06 UTC 2023 , Edited by admin on Sat Dec 16 14:18:06 UTC 2023
PRIMARY
Sugar Site Range Site Count
2'-O-Methoxyethyl ribose 1_1-1_5;1_16-1_20 10 / 20
Deoxyribose (DNA) 1_6-1_15 10 / 20
Linkage Site Range Site Count
Phosporothioate 1_1-1_20 20 / 19