Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Sat Dec 16 18:28:01 UTC 2023
by
admin
on
Sat Dec 16 18:28:01 UTC 2023
|
| Source Materials Class | ORGANISM |
| Source Materials Type | AUTOLOGOUS HUMAN |
| Source Materials State | LIVE GENETICALLY MODIFIED |
| Source Materials Parent | |
| Part | BONE MARROW |
| Fraction Name | CD34+ cells isolated from bone marrow of newly diagnosed X-linked severe combined immunodeficiency (X-SCID) patients |
| Record UNII |
XH2XT2GQS6
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Official Name | English | ||
|
Common Name | English | ||
|
Common Name | English |
| Classification Tree | Code System | Code | ||
|---|---|---|---|---|
|
FDA ORPHAN DRUG |
759720
Created by
admin on Sat Dec 16 18:28:01 UTC 2023 , Edited by admin on Sat Dec 16 18:28:01 UTC 2023
|
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
|
XH2XT2GQS6
Created by
admin on Sat Dec 16 18:28:01 UTC 2023 , Edited by admin on Sat Dec 16 18:28:01 UTC 2023
|
PRIMARY | |||
|
11551
Created by
admin on Sat Dec 16 18:28:01 UTC 2023 , Edited by admin on Sat Dec 16 18:28:01 UTC 2023
|
PRIMARY | |||
|
C184824
Created by
admin on Sat Dec 16 18:28:01 UTC 2023 , Edited by admin on Sat Dec 16 18:28:01 UTC 2023
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
EXPRESSED PROTEIN->VECTOR |
|
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
ACTIVE MOIETY |
|
Agent Modifications
| Modification Process | Modification Role | Modification Type | Amount | Fragment Name | Fragment ID |
|---|---|---|---|---|---|
| LENTIVIRAL TRANSFECTION | TRANSFECTION | FIROLIMOGENE AUTOTEMCEL VECTOR | PZ6C5A9U4S |
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| VECTOR EXPRESSED PROTEIN | CYTOKINE RECEPTOR COMMON SUBUNIT GAMMA | OX7CIS4H0Z | ||||
| INSERTED GENE EXPRESSION VECTOR | FIROLIMOGENE AUTOTEMCEL TRANSGENE INSERT | 73GRS55F42 |