BEVUFENOGENE NOFEPARVOVEC

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Sat Dec 16 16:34:20 GMT 2023` Edited by `admin` on `Sat Dec 16 16:34:20 GMT 2023`
Source Materials Class	ORGANISM
Source Materials Type	RECOMBINANT VIRUS
Source Materials State	LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family	Parvoviridae
Organism Genus	Dependovirus
Organism Species	adeno-associated virus
Author	NONE
Infraspecific Type	TRANSGENIC
Infraspecific Name	AAV2/5-HRKP.RPGR
Part	WHOLE
Record UNII	W6GL3Z8KWT
Record Status	`Validated (UNII)`
Record Version

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Name

Type

Language

BEVUFENOGENE NOFEPARVOVEC

Official Name

English

DNA (RECOMBINANT HUMAN HEMATOPOIETIC STEM CELL-DERIVED ADENO-ASSOCIATED VIRUS VECTOR SEROTYPE AAVHSC15 HUMAN LIVER-SPECIFIC EXPRESSION CASSETTE INCLUDING HUMAN PHENYLALANINE 4-HYDROXYLASE CODON-OPTIMIZED CDNA PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMIN

Common Name

English

A NON-REPLICATING, RECOMBINANT ADENO-ASSOCIATED VIRUS, HEMATOPOIETIC STEM CELL SEROTYPE 15 (AAVHSC15) EXPRESSING CODON-OPTIMISED HUMAN PHENYLALANINE HYDROXYLASE (PAH) UNDER CONTROL OF A LIVER-SPECIFIC HYBRID PROMOTER (COMPRISING HUMAN HEPATIC CONTROL REG

Common Name

English

bevufenogene nofeparvovec [INN]

Common Name

English

HMI-102

Code

English

BEVUFENOGENE NOFEPARVOVEC [USAN]

Common Name

English

Code System Code Type Description

USAN

JK-252