IFEZUNTIRGENE INILPARVOVEC

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Wed Apr 02 05:46:06 GMT 2025` Edited by `admin` on `Wed Apr 02 05:46:06 GMT 2025`
Source Materials Class	ORGANISM
Source Materials Type	RECOMBINANT VIRUS
Source Materials State	LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family	Parvoviridae
Organism Genus	Dependoparvovirus
Organism Species	adeno-associated dependoparvovirus
Infraspecific Type	RECOMBINANT VECTOR
Infraspecific Name	AAV5-ENCODING A MICRORNA TARGETED TO EXON 1 OF THE HUMAN HUNTINGTIN GENE
Part	whole
Record UNII	VB2ZC1P6P4
Record Status	`Validated (UNII)`
Record Version

Download

Name

Type

Language

IFEZUNTIRGENE INILPARVOVEC

Official Name

English

A RECOMBINANT, REPLICATION DEFICIENT ADENO-ASSOCIATED VIRUS SEROTYPE 5 (AAV5) VECTOR ENCODING A MICRORNA (MIRNA) TARGETING THE EXON 1 OF HUMAN HUNTINGTIN PROTEIN (HTT) MRNA (MIHTT). THE EXPRESSION CASSETTE CONSISTS OF A CHIMERIC CHICKEN BETA-ACTIN PROMOT

Preferred Name

English

DNA (RECOMBINANT REPLICATION-DEFICIENT ADENO-ASSOCIATED VIRUS 5 VECTOR AMT-130 CHICKEN .BETA.-ACTIN PROMOTER PLUS HUMAN HUNTINGTIN MRNA-TARGETING MICRORNA MIHTT-SPECIFYING)

Common Name

English

ifezuntirgene inilparvovec [INN]

Common Name

English

Code System Code Type Description

CLINICAL_TRIALS.GOV

NCT04120493