U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 18:36:03 GMT 2023
Edited
by admin
on Sat Dec 16 18:36:03 GMT 2023
Source Materials Class ORGANISM
Source Materials Type AUTOLOGOUS HUMAN
Source Materials State LIVE ATTENUATED GENETICALLY MODIFIED
Source Materials Parent
Part BLOOD
Fraction Name Hematopoietic cells
Record UNII
RD86XHH46N
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Marnetegragene Autotemcel
INN   USAN  
Official Name English
RP-L201 (CELL THERAPY PRODUCT WHICH CONSISTS OF AUTOLOGOUS GENETICALLY MODIFIED CD34+ HEMATOPOIETIC CELLS WHICH ARE TRANSDUCED WITH A LENTIVIRAL VECTOR (LV) (CHIM-CD18-WPRE LV) THAT ENCODES FOR THE CD18 .BETA.-SUBUNIT OF HUMAN .BETA.2 INTEGRINS (ITGB2 GE
Common Name English
MARNETEGRAGENE AUTOTEMCEL [USAN]
Common Name English
LADICELL
Brand Name English
marnetegragene autotemcel [INN]
Common Name English
RP-L201
Code English
Code System Code Type Description
NCI_THESAURUS
C180650
Created by admin on Sat Dec 16 18:36:03 GMT 2023 , Edited by admin on Sat Dec 16 18:36:03 GMT 2023
PRIMARY
FDA UNII
RD86XHH46N
Created by admin on Sat Dec 16 18:36:03 GMT 2023 , Edited by admin on Sat Dec 16 18:36:03 GMT 2023
PRIMARY
USAN
HI-198
Created by admin on Sat Dec 16 18:36:03 GMT 2023 , Edited by admin on Sat Dec 16 18:36:03 GMT 2023
PRIMARY
INN
11717
Created by admin on Sat Dec 16 18:36:03 GMT 2023 , Edited by admin on Sat Dec 16 18:36:03 GMT 2023
PRIMARY
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
VECTOR EXPRESSED PROTEIN INTEGRIN BETA-2 TIW6JAG30P
INSERTED GENE EXPRESSION VECTOR UNSPECIFIED SUBSTANCE
4329fb84
(not in database)
Name Property Type Amount Referenced Substance Defining Parameters References
ANTIGEN EXPRESSED BIOLOGICAL