U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Source Materials Class ORGANISM
Source Materials Type VIRUS
Source Materials State LIVE GENETICALLY MODIFIED NON-REPLICATING
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name AAV-9/SMN RECOMBINANT
Part WHOLE
Record UNII
MLU3LU3EVV
Record Status Validated (UNII)
Record Version

Structural Modifications