U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 12:59:38 GMT 2025
Edited
by admin
on Wed Apr 02 12:59:38 GMT 2025
Nucleic Acid Type RNAI
Sequence Type COMPLETE
Record UNII
8QFS4BAH6H
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
COTSIRANIB TGF-.BETA.1 SI-RNA COMPONENT
Preferred Name English
Pixofisiran sodium
Common Name English
RNA, (A-G-A-A-G-U-U-G-G-C-A-U-G-G-U-A-G-C-C-C-U-U-G-G-G), COMPLEX WITH RNA (C-C-C-A-A-G-G-G-C-U-A-C-C-A-U-G-C-C-A-A-C-U-U-C-U) SODIUM (1:1:48)
Common Name English
HIMTF-25-2
Common Name English
STP-705 COMPONENT TGF-.BETA.1 SI-RNA
Common Name English
RNA, (C-C-C-A-A-G-G-G-C-U-A-C-C-A-U-G-C-C-A-A-C-U-U-C-U)/~2 RNA, (A-G-A-A-G-U-U-G-G-C-A-U-G-G-U-A-G-C-C-C-U-U-G-G-G)
Common Name English
Code System Code Type Description
SMS_ID
300000039068
Created by admin on Wed Apr 02 12:59:38 GMT 2025 , Edited by admin on Wed Apr 02 12:59:38 GMT 2025
PRIMARY
FDA UNII
8QFS4BAH6H
Created by admin on Wed Apr 02 12:59:38 GMT 2025 , Edited by admin on Wed Apr 02 12:59:38 GMT 2025
PRIMARY
Sugar Site Range Site Count
D-Ribose (RNA) 1_1-1_25;2_1-2_25 50 / 50
Linkage Site Range Site Count
1_2-1_25;2_2-2_25 48 / 48
Related Record Type Details
PARENT -> SALT/SOLVATE
Related Record Type Details
ACTIVE MOIETY
Name Property Type Amount Referenced Substance Defining Parameters References
MOL_WEIGHT:NUMBER(CALCULATED) CHEMICAL