U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS
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Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 00:58:06 GMT 2025
Edited
by admin
on Wed Apr 02 00:58:06 GMT 2025
Nucleic Acid Type siRNA
Sequence Type COMPLETE
Record UNII
O5QC3YP0M7
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Pixofisiran
INN  
Official Name English
COTSIRANIB TGF-.BETA.1 SI-RNA FREE ACID COMPONENT
Preferred Name English
HIMTF-25-2 FREE ACID
Common Name English
pixofisiran [INN]
Common Name English
STP-705 COMPONENT TGF-.BETA.1 SI-RNA FREE ACID
Common Name English
RNA, (A-G-A-A-G-U-U-G-G-C-A-U-G-G-U-A-G-C-C-C-U-U-G-G-G), COMPLEX WITH RNA (C-C-C-A-A-G-G-G-C-U-A-C-C-A-U-G-C-C-A-A-C-U-U-C-U) (1:1)
Common Name English
Code System Code Type Description
INN
11789
Created by admin on Wed Apr 02 00:58:06 GMT 2025 , Edited by admin on Wed Apr 02 00:58:06 GMT 2025
PRIMARY
FDA UNII
O5QC3YP0M7
Created by admin on Wed Apr 02 00:58:06 GMT 2025 , Edited by admin on Wed Apr 02 00:58:06 GMT 2025
PRIMARY
CAS
1152798-48-5
Created by admin on Wed Apr 02 00:58:06 GMT 2025 , Edited by admin on Wed Apr 02 00:58:06 GMT 2025
PRIMARY
NCI_THESAURUS
C184821
Created by admin on Wed Apr 02 00:58:06 GMT 2025 , Edited by admin on Wed Apr 02 00:58:06 GMT 2025
PRIMARY
SMS_ID
300000039067
Created by admin on Wed Apr 02 00:58:06 GMT 2025 , Edited by admin on Wed Apr 02 00:58:06 GMT 2025
PRIMARY
Sugar Site Range Site Count
D-Ribose (RNA) 1_1-1_25;2_1-2_25 50 / 50
Linkage Site Range Site Count
Phosphate 1_2-1_25;2_2-2_25 48 / 48
Related Record Type Details
SALT/SOLVATE -> PARENT
TARGET->INHIBITOR OF EXPRESSION
Related Record Type Details
ACTIVE MOIETY
Name Property Type Amount Referenced Substance Defining Parameters References
MOL_WEIGHT:NUMBER(CALCULATED) CHEMICAL