U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 06:49:24 GMT 2025
Edited
by admin
on Wed Apr 02 06:49:24 GMT 2025
Source Materials Class ORGANISM
Source Materials Type AUTOLOGOUS HUMAN
Source Materials State LIVE GENETICALLY MODIFIED
Source Materials Parent
Part blood cell
Fraction Name t cells
Record UNII
760HJB0YRD
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
OBECABTAGENE AUTOLEUCEL
INN  
Official Name English
AUTO-1
Preferred Name English
AUTOLOGOUS CD4+ AND CD8+ T CELLS, ENRICHED FROM PERIPHERAL BLOOD MONONUCLEAR CELLS (PBMCS) OBTAINED BY APHERESIS TRANSDUCED EX VIVO WITH A NON-REPLICATING, SELF-INACTIVATING (SIN) LENTIVIRAL VECTOR, ENCODING A CHIMERIC ANTIGEN RECEPTOR (CAR) CONSISTING O
Common Name English
OBECABTAGENE AUTOLEUCEL [USAN]
Common Name English
AUTO1
Code English
Obecabtagene autoleucel [WHO-DD]
Common Name English
SELF-INACTIVATING LENTIVIRAL VECTOR CONSISTING OF 5' FUSION BETWEEN THE CMV PROMOTER AND HIV LTR, WHERE THE CMV PROMOTER REPLACES THE U3 REGION. PACKAGING SIGNAL (.PSI.), THE REV RESPONSIVE ELEMENT (RRE) AND THE CENTRAL POLYPURINE TRACT (CPPT) ARE RETAIN
Common Name English
obecabtagene autoleucel [INN]
Common Name English
Code System Code Type Description
FDA UNII
760HJB0YRD
Created by admin on Wed Apr 02 06:49:24 GMT 2025 , Edited by admin on Wed Apr 02 06:49:24 GMT 2025
PRIMARY
SMS_ID
300000000500
Created by admin on Wed Apr 02 06:49:24 GMT 2025 , Edited by admin on Wed Apr 02 06:49:24 GMT 2025
PRIMARY
NCI_THESAURUS
C172746
Created by admin on Wed Apr 02 06:49:24 GMT 2025 , Edited by admin on Wed Apr 02 06:49:24 GMT 2025
PRIMARY
INN
11486
Created by admin on Wed Apr 02 06:49:24 GMT 2025 , Edited by admin on Wed Apr 02 06:49:24 GMT 2025
PRIMARY
USAN
JK-262
Created by admin on Wed Apr 02 06:49:24 GMT 2025 , Edited by admin on Wed Apr 02 06:49:24 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
VECTOR EXPRESSED PROTEIN OBECABTAGENE AUTOLEUCEL CHIMERIC ANTIGEN RECEPTOR PREPROTEIN Y96BQ8R24J
VECTOR EXPRESSED PROTEIN OBECABTAGENE AUTOLEUCEL CHIMERIC ANTIGEN RECEPTOR Z7MN57NAL9
INSERTED GENE EXPRESSION VECTOR OBECABTAGENE AUTOLEUCEL LENTIVIRAL VECTOR TRANSGENE INSERT 93SKR9HJ3R