Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 00:45:12 GMT 2025
by
admin
on
Wed Apr 02 00:45:12 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependovirus |
| Organism Species | adeno-associated virus |
| Author | NONE |
| Infraspecific Type | SUBSTRAIN |
| Infraspecific Name | AAV2(ITR)/AAV1, 2, 3B, 4, 5, 6 8, 9, AVIAN AND BOVINE AAV(PALSMID) FOLLOWED BY IN VIVOSELECTION IN FAH//RAG2//IL2RG/ (FRG) MICE PARTIALLY REPOPULATED WITH HUMAN HEPATOCYTES/HUMAN B-DOMAIN-DELETED BLOOD COAGULATION FACTOR VIII/TTRM/VECTOR (INTRONLESS) |
| Part | whole |
| Record UNII |
63QD0BX9B4
|
| Record Status |
Validated (UNII)
|
| Record Version |
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-
Download
| Name | Type | Language | ||
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Official Name | English | ||
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Preferred Name | English | ||
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Systematic Name | English |
| Code System | Code | Type | Description | ||
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63QD0BX9B4
Created by
admin on Wed Apr 02 00:45:12 GMT 2025 , Edited by admin on Wed Apr 02 00:45:12 GMT 2025
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C175201
Created by
admin on Wed Apr 02 00:45:12 GMT 2025 , Edited by admin on Wed Apr 02 00:45:12 GMT 2025
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10992
Created by
admin on Wed Apr 02 00:45:12 GMT 2025 , Edited by admin on Wed Apr 02 00:45:12 GMT 2025
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2163074-26-6
Created by
admin on Wed Apr 02 00:45:12 GMT 2025 , Edited by admin on Wed Apr 02 00:45:12 GMT 2025
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300000039221
Created by
admin on Wed Apr 02 00:45:12 GMT 2025 , Edited by admin on Wed Apr 02 00:45:12 GMT 2025
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PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
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TARGET->ENZYME REPLACEMENT |
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DERIVATIVE -> PARENT |
| Related Record | Type | Details | ||
|---|---|---|---|---|
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ACTIVE MOIETY |
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| GENE_EXPRESSION VECTOR | ROVOCTOCOGENE DURPARVOVEC TRANSGENE INSERT | UI9IU8M1ME |