U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 13:12:57 GMT 2025
Edited
by admin
on Wed Apr 02 13:12:57 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependovirus
Organism Species adeno-associated virus
Infraspecific Type SUBSTRAIN
Infraspecific Name Recombinant AAV2/6 Vector ApoE/hAAT/Encoding the cDNA for hGLA (ST-920)
Part whole
Record UNII
3U2455CVM6
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
ST-920
Preferred Name English
ISARALGAGENE CIVAPARVOVEC
INN  
Official Name English
isaralgagene civaparvovec [INN]
Common Name English
A RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE 6 (AAV6) ENCODING CODON-OPTIMISED HUMAN ALPHA-GALACTOSIDASE A (GLA) UNDER CONTROL OF LIVER-SPECIFIC REGULATORY ELEMENTS (COMPRISING ENHANCER AND HEPATIC CONTROL REGION FROM THE HUMAN A
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR ST-920 LIVER-SPECIFIC ENHANCER-PROMOTER-INTRON REGULATORY MODULE PLUS HUMAN .ALPHA.-GALACTOSIDASE PRECURSOR-SPECIFYING)
Common Name English
ST920
Code English
Code System Code Type Description
NCI_THESAURUS
C179094
Created by admin on Wed Apr 02 13:12:57 GMT 2025 , Edited by admin on Wed Apr 02 13:12:57 GMT 2025
PRIMARY
FDA UNII
3U2455CVM6
Created by admin on Wed Apr 02 13:12:57 GMT 2025 , Edited by admin on Wed Apr 02 13:12:57 GMT 2025
PRIMARY
CAS
2378601-29-5
Created by admin on Wed Apr 02 13:12:57 GMT 2025 , Edited by admin on Wed Apr 02 13:12:57 GMT 2025
PRIMARY
INN
11536
Created by admin on Wed Apr 02 13:12:57 GMT 2025 , Edited by admin on Wed Apr 02 13:12:57 GMT 2025
PRIMARY INN
SMS_ID
300000001040
Created by admin on Wed Apr 02 13:12:57 GMT 2025 , Edited by admin on Wed Apr 02 13:12:57 GMT 2025
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR UNSPECIFIED SUBSTANCE
fb56e2b3
(not in database)