U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 19:11:26 UTC 2023
Edited
by admin
on Sat Dec 16 19:11:26 UTC 2023
Source Materials Class ORGANISM
Source Materials Type AUTOLOGOUS HUMAN
Source Materials State LIVE
Source Materials Parent
Part BLOOD
Fraction Material Type CELLS
Fraction Name T CELLS
Record UNII
33KHD8ZZ8Y
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
ACMUCABTAGENE AUTOLEUCEL
INN  
Official Name English
AUTOLOGOUS T CELLS OBTAINED FROM PERIPHERAL BLOOD MONONUCLEAR CELLS BY LEUKAPHERESIS, TRANSDUCED WITH A SELFINACTIVATING, NON-REPLICATING LENTIVIRAL VECTOR, ENCODING A CHIMERIC ANTIGEN RECEPTOR (CAR) TARGETING B-LYMPHOCYTE ANTIGEN CD19 (ALSO KNOWN AS B-L
Common Name English
acmucabtagene autoleucel [INN]
Common Name English
Code System Code Type Description
INN
11832
Created by admin on Sat Dec 16 19:11:26 UTC 2023 , Edited by admin on Sat Dec 16 19:11:26 UTC 2023
PRIMARY
FDA UNII
33KHD8ZZ8Y
Created by admin on Sat Dec 16 19:11:26 UTC 2023 , Edited by admin on Sat Dec 16 19:11:26 UTC 2023
PRIMARY
Related Record Type Details
TARGET->CYTOTOXIC T-CELL
Related Record Type Details
ACTIVE MOIETY

Agent Modifications

Modification Process Modification Role Modification Type Amount Fragment Name Fragment ID
CULTURE HUMAN INTERLEUKIN-2 FNO32LO217
LENTIVIRAL TRANSFECTION TRANSFECTION ACMUCABTAGENE AUTOLEUCEL VECTOR UG6BGQ2UWP
CULTURE ACTIVATOR UNSPECIFIED SUBSTANCE a64e131d
CULTURE INTERLEUKIN-7 HUMAN RECOMBINANT 418XB47Y71

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
VECTOR EXPRESSED PROTEIN ACMUCABTAGENE AUTOLEUCEL EXPRESSED PROTEIN T47V958ZJ3
INSERTED GENE EXPRESSION VECTOR ACMUCABTAGENE AUTOLEUCEL TRANSGENE INSERT 4EDN5ZS6P9
Name Property Type Amount Referenced Substance Defining Parameters References
ANTIGEN EXPRESSED BIOLOGICAL
ANTIGEN EXPRESSED BIOLOGICAL