U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 03:25:17 GMT 2025
Edited
by admin
on Wed Apr 02 03:25:17 GMT 2025
Source Materials Class ORGANISM
Source Materials Type VIRUS
Source Materials State LIVE GENETICALLY MODIFIED NON-REPLICATING
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SEROTYPE
Infraspecific Name SEROTYPE RH74
Part whole
Record UNII
2P6QV2ZE52
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS AAVRH74 VECTOR SRP-9001 MHCK7 PROMOTER PLUS MICRO-DYSTROPHIN-SPECIFYING)
Preferred Name English
DELANDISTROGENE MOXEPARVOVEC
USAN   INN  
Official Name English
SRP-9001
Code English
Delandistrogene moxeparvovec [WHO-DD]
Common Name English
delandistrogene moxeparvovec [INN]
Common Name English
DELANDISTROGENE MOXEPARVOVEC [USAN]
Common Name English
Code System Code Type Description
DAILYMED
2P6QV2ZE52
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
SMS_ID
100000183376
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
USAN
HI-01
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
WIKIPEDIA
Adeno-associated_virus
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
NCI_THESAURUS
C177062
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
FDA UNII
2P6QV2ZE52
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
CAS
2305040-16-6
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
INN
11631
Created by admin on Wed Apr 02 03:25:17 GMT 2025 , Edited by admin on Wed Apr 02 03:25:17 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR UNSPECIFIED SUBSTANCE
37b3186d
(not in database)