Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 10:41:03 GMT 2025
by
admin
on
Wed Apr 02 10:41:03 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | AUTOLOGOUS HUMAN |
| Source Materials State | LIVE GENETICALLY MODIFIED |
| Source Materials Parent | |
| Part | mobilised peripheral blood, from patients with sickle cell disease |
| Fraction Material Type | cells |
| Fraction Name | hematopoietic stem and progenitor cells (patients with sickle cell disease) |
| Record UNII |
2C6A9NH2Z8
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
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Preferred Name | English | ||
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Official Name | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Code | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
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HI-143
Created by
admin on Wed Apr 02 10:41:03 GMT 2025 , Edited by admin on Wed Apr 02 10:41:03 GMT 2025
|
PRIMARY | |||
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C176855
Created by
admin on Wed Apr 02 10:41:03 GMT 2025 , Edited by admin on Wed Apr 02 10:41:03 GMT 2025
|
PRIMARY | |||
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11826
Created by
admin on Wed Apr 02 10:41:03 GMT 2025 , Edited by admin on Wed Apr 02 10:41:03 GMT 2025
|
PRIMARY | |||
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300000035100
Created by
admin on Wed Apr 02 10:41:03 GMT 2025 , Edited by admin on Wed Apr 02 10:41:03 GMT 2025
|
PRIMARY | |||
|
2C6A9NH2Z8
Created by
admin on Wed Apr 02 10:41:03 GMT 2025 , Edited by admin on Wed Apr 02 10:41:03 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
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ACTIVE MOIETY |
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Agent Modifications
| Modification Process | Modification Role | Modification Type | Amount | Fragment Name | Fragment ID |
|---|---|---|---|---|---|
| CD34+ Cell Labeling | IMMUNOLOGICAL | ||||
| LENTIVIRAL TRANSFECTION | BETIBEGLOGENE DAROLENTIVEC | 7VEJ4HT24J | |||
| CD34+ Enrichment | CELL SEPARATION |
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| VECTOR EXPRESSED PROTEIN | UNSPECIFIED SUBSTANCE |
f4353dfd
(not in database)
|
||||
| INSERTED GENE EXPRESSION VECTOR | UNSPECIFIED SUBSTANCE |
53ad4970
(not in database)
|
| Name | Property Type | Amount | Referenced Substance | Defining | Parameters | References |
|---|---|---|---|---|---|---|
| ANTIGEN EXPRESSED | BIOLOGICAL |
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