U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
Esonadogene Imvoparvovec
INN  
Official Name English
DNA (recombinant replication-defective adeno-associated virus 2 vector NFS01 human cytomegalovirus enhancer plus human cytomegalovirus promoter plus Macacine herpesvirus 3 chimeric intron plus human heme A farnesyltransferase gene COX10 mitochondrial tar
Preferred Name English
recombinant, non-replicating adeno-associated virus serotype 2 (AAV2) vector encoding codon-optimised human NADH dehydrogenase subunit 4 (also known as NADH-ubiquinone oxidoreductase chain 4; MTND4, NADH4, ND4) preceded by a Kozak sequence and a mitochon
Common Name English
esonadogene imvoparvovec [INN]
Common Name English
Code System Code Type Description
SMS_ID
300000037246
Created by admin on Wed Apr 02 17:47:10 GMT 2025 , Edited by admin on Wed Apr 02 17:47:10 GMT 2025
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FDA UNII
Z57CL8M2AE
Created by admin on Wed Apr 02 17:47:10 GMT 2025 , Edited by admin on Wed Apr 02 17:47:10 GMT 2025
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NCI_THESAURUS
C199044
Created by admin on Wed Apr 02 17:47:10 GMT 2025 , Edited by admin on Wed Apr 02 17:47:10 GMT 2025
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INN
12424
Created by admin on Wed Apr 02 17:47:10 GMT 2025 , Edited by admin on Wed Apr 02 17:47:10 GMT 2025
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CAS
2678565-23-4
Created by admin on Wed Apr 02 17:47:10 GMT 2025 , Edited by admin on Wed Apr 02 17:47:10 GMT 2025
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