U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
ADLINACOGENE CIVAPARVOVEC TRANSGENE INSERT
Common Name English
PROMOTERLESS HUMAN COAGULATION FACTOR IX (HF9, FACTOR IX OR FIX) TRANSGENE CASSETTE, ENCODING EXONS 2-8 AND SPLICE ACCEPTOR SITE SEQUENCE (SA) FROM HF9 EXON 2, FLANKED BY A SEQUENCE HOMOLOGOUS TO THE ZINC-FINGER NUCLEASE (ZFN) CLEAVAGE SITE OF THE HUMAN
Preferred Name English
Code System Code Type Description
FDA UNII
UM90H33QOQ
Created by admin on Wed Apr 02 06:15:09 GMT 2025 , Edited by admin on Wed Apr 02 06:15:09 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_2474 2474 / 2474
Linkage Site Range Site Count
Phosphate 1_1-1_2474 2474 / 2473