U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
ZAFTUCLENEGENE PIRUPARVOVEC TRANSGENE INSERT
Common Name English
ZAFTUCLENEGENE PIRUPARVOVEC TRANSGENE INSERT (CODON-OPTIMISED HUMAN PALMITOYL-PROTEIN THIOESTERASE 1 (PPT1, CLN1), UNDER THE CONTROL OF A SYNTHETIC PROMOTER CONSISTING OF A CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN .BETA.-ACTIN (CBA) PROMOTER AND A HYBRID I
Common Name English
Code System Code Type Description
FDA UNII
UA46HCC58W
Created by admin on Sat Dec 16 18:42:46 GMT 2023 , Edited by admin on Sat Dec 16 18:42:46 GMT 2023
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_4507 4507 / 4507
Linkage Site Range Site Count
Phosphate 1_2-1_4507 4506 / 4506