U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

2019
334
Name Type Language
ONASEMNOGENE ABEPARVOVEC
INN   USAN  
Official Name English
ZOLGENSMA
Preferred Name English
DNA (SYNTHETIC ADENO-ASSOCIATED VIRUS 9 VECTOR SCAAV9.CB.HSMN HUMAN SURVIVOR MOTOR NEURON PROTEIN-SPECIFYING)
Systematic Name English
NON-REPLICATING RECOMBINANT SELF-COMPLEMENTARY (SC) ADENO-ASSOCIATED VIRUS SEROTYPE 9 (AAV9) VECTOR CONTAINING THE CDNA OF THE SURVIVAL OF MOTOR NEURON 2 (SMN2) GENE UNDER THE CONTROL OF THE HYBRID CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN BETA-ACTIN PROMOT
Common Name English
ONASEMNOGENE ABEPARVOVEC [USAN]
Common Name English
AVXS-101
Code English
Onasemnogene abeparvovec [WHO-DD]
Common Name English
ONASEMNOGENE ABEPARVOVEC [MI]
Common Name English
onasemnogene abeparvovec [INN]
Common Name English
Classification Tree Code System Code
FDA ORPHAN DRUG 444714
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
Code System Code Type Description
SMS_ID
100000177723
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
DRUG CENTRAL
5332
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
DRUG BANK
DB15528
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
WIKIPEDIA
Onasemnogene abeparvovec
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
INN
10619
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
CAS
1922968-73-7
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
USAN
EF-126
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
MERCK INDEX
m12206
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
FDA UNII
MLU3LU3EVV
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
NCI_THESAURUS
C174715
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
RXCUI
2170226
Created by admin on Wed Apr 02 01:43:26 GMT 2025 , Edited by admin on Wed Apr 02 01:43:26 GMT 2025
PRIMARY
NIH
NCATS
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DISCLAIMER
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National Center for Advancing Translational Sciences (NCATS),
6701 Democracy Boulevard, Bethesda MD 20892-4874 • 301-594-8966