U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
Tremtelectogene Empogeditemcel
Code English
allogeneic human CD34 + hematopoietic stem and progenitor cells (HSPC) obtained from peripheral blood by leukapheresis from human leukocyte antigen (HLA)-matched healthy donors, genetically modified ex vivo by CRISPR/Cas9 (clustered regularly interspaced
Preferred Name English
tremtelectogene empogeditemcel [INN]
Common Name English
Code System Code Type Description
SMS_ID
300000049566
Created by admin on Wed Apr 02 12:12:44 GMT 2025 , Edited by admin on Wed Apr 02 12:12:44 GMT 2025
PRIMARY
INN
12263
Created by admin on Wed Apr 02 12:12:44 GMT 2025 , Edited by admin on Wed Apr 02 12:12:44 GMT 2025
PRIMARY
FDA UNII
CT5FM8JN3S
Created by admin on Wed Apr 02 12:12:44 GMT 2025 , Edited by admin on Wed Apr 02 12:12:44 GMT 2025
PRIMARY
NCI_THESAURUS
C180524
Created by admin on Wed Apr 02 12:12:44 GMT 2025 , Edited by admin on Wed Apr 02 12:12:44 GMT 2025
PRIMARY