U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
A RECOMBINANT, NON-REPLICATING, ADENO-ASSOCIATED VIRUS SEROTYPE HU37 (AAVHU37) VECTOR, ENCODING A CODON-OPTIMISED B-DOMAIN DELETED SQ VARIANT OF HUMAN BLOOD-COAGULATION FACTOR VIII (HFVIII-SQ), UNDER THE CONTROL OF A HYBRID LIVER PROMOTER (MUS MUSCULUS T
Preferred Name English
PEBOCTOCOGENE CAMAPARVOVEC
INN  
Official Name English
peboctocogene camaparvovec [INN]
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS HU37 VECTOR DTX201 MUS MUSCULUS TRANSTHYRETIN ENHANCER-HUMAN TRANSTHYRETIN PROMOTER PLUS HUMAN (1-764)-(1659-2351)-BLOOD-COAGULATION FACTOR VIII-SPECIFYING)
Common Name English
Code System Code Type Description
INN
11667
Created by admin on Wed Apr 02 06:33:54 GMT 2025 , Edited by admin on Wed Apr 02 06:33:54 GMT 2025
PRIMARY INN
CAS
2408734-39-2
Created by admin on Wed Apr 02 06:33:54 GMT 2025 , Edited by admin on Wed Apr 02 06:33:54 GMT 2025
PRIMARY
NCI_THESAURUS
C179113
Created by admin on Wed Apr 02 06:33:54 GMT 2025 , Edited by admin on Wed Apr 02 06:33:54 GMT 2025
PRIMARY
SMS_ID
100000178167
Created by admin on Wed Apr 02 06:33:54 GMT 2025 , Edited by admin on Wed Apr 02 06:33:54 GMT 2025
PRIMARY
FDA UNII
CFE96HL6SK
Created by admin on Wed Apr 02 06:33:54 GMT 2025 , Edited by admin on Wed Apr 02 06:33:54 GMT 2025
PRIMARY