A RECOMBINANT, NON-REPLICATING, ADENO-ASSOCIATED VIRUS SEROTYPE HU37 (AAVHU37) VECTOR, ENCODING A CODON-OPTIMISED B-DOMAIN DELETED SQ VARIANT OF HUMAN BLOOD-COAGULATION FACTOR VIII (HFVIII-SQ), UNDER THE CONTROL OF A HYBRID LIVER PROMOTER (MUS MUSCULUS T
Preferred Name
English
PEBOCTOCOGENE CAMAPARVOVEC
Official Name
English
peboctocogene camaparvovec [INN]
Common Name
English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS HU37 VECTOR DTX201 MUS MUSCULUS TRANSTHYRETIN ENHANCER-HUMAN TRANSTHYRETIN PROMOTER PLUS HUMAN (1-764)-(1659-2351)-BLOOD-COAGULATION FACTOR VIII-SPECIFYING)
