U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
ZILEBESIRAN SODIUM
USAN  
Official Name English
RNA, (Gm-sp-Um-sp-Cm-Am-Um-Cm-(2'-deoxy-2'-fluoro)C-Am-(2'-deoxy-2'-fluoro)C- (2'-deoxy-2'-fluoro)A-(2'-deoxy-2'-fluoro)A-Um-Gm-Am-Gm-Am-Gm-Um-Am-Cm-Am), 3'-[[(2S,4R)-1-[29-[[2-(acetylamino)-2-deoxy-β-D-galactopyranosyl]oxy]-14,14-bis[[3-[[3- [[5-[[2-(a
Common Name English
[(2S,4R)-1-{1-[(2-acetamido-2-deoxy-β-D-galactopyranosyl)oxy]-16,16-bis({3-[(3-{5-[(2- acetamido-2-deoxy-β-D-galactopyranosyl)oxy]pentanamido}propyl)amino]-3- oxopropoxy}methyl)-5,11,18-trioxo-14-oxa-6,10,17- triazanonacosan-29-oyl}-4- hydroxypyrrolidi
Common Name English
ZILEBESIRAN SODIUM [USAN]
Common Name English
ALN-AGT01 SODIUM
Code English
Code System Code Type Description
NCI_THESAURUS
C188750
Created by admin on Sat Dec 16 18:44:18 GMT 2023 , Edited by admin on Sat Dec 16 18:44:18 GMT 2023
PRIMARY
USAN
KL-81
Created by admin on Sat Dec 16 18:44:18 GMT 2023 , Edited by admin on Sat Dec 16 18:44:18 GMT 2023
PRIMARY
FDA UNII
A8P3J9MPQ3
Created by admin on Sat Dec 16 18:44:18 GMT 2023 , Edited by admin on Sat Dec 16 18:44:18 GMT 2023
PRIMARY
CAS
2380166-34-5
Created by admin on Sat Dec 16 18:44:18 GMT 2023 , Edited by admin on Sat Dec 16 18:44:18 GMT 2023
PRIMARY
Sugar Site Range Site Count
2'-Fluoro-Ribose 1_2;1_14;1_16;2_7;2_9-2_11 7 / 44
2'-O-Methyl-Ribose 1_1;1_3-1_13;1_15;1_17-1_23;2_1-2_6;2_8;2_12-2_21 37 / 44
Linkage Site Range Site Count
Sodium Phosporothioate 1_2-1_3;1_22-1_23;2_2-2_3 6 / 42
1_4-1_21;2_4-2_21 36 / 42