U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
LIXMABEGAGENE RELDUPARVOVEC
INN  
Official Name English
A RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE RH.10 (RAAVRH.10) VECTOR ENCODING HUMAN .BETA.-GALACTOSIDASE (GLB1), UNDER CONTROL OF THE SYNTHETIC CAG PROMOTER (CMV IMMEDIATE-EARLY ENHANCER/CHICKEN .BETA.-ACTIN (CB) PROMOTER, CHICKEN .BET
Common Name English
LYS-GM101
Code English
lixmabegagene relduparvovec [INN]
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR LYS-GM101 SYNTHETIC CAG PROMOTER PLUS HUMAN .BETA.-GALACTOSIDASE TRANSGENE PLUS HUMAN GROWTH HORMONE POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS-SPECIFYING)
Common Name English
Code System Code Type Description
INN
11919
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY
NCI_THESAURUS
C188537
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY
CAS
2461531-19-9
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY
FDA UNII
8G4FJ7F8EY
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY