A RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE RH.10 (RAAVRH.10) VECTOR ENCODING HUMAN .BETA.-GALACTOSIDASE (GLB1), UNDER CONTROL OF THE SYNTHETIC CAG PROMOTER (CMV IMMEDIATE-EARLY ENHANCER/CHICKEN .BETA.-ACTIN (CB) PROMOTER, CHICKEN .BET
Common Name
English
lixmabegagene relduparvovec [INN]
Common Name
English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR LYS-GM101 SYNTHETIC CAG PROMOTER PLUS HUMAN .BETA.-GALACTOSIDASE TRANSGENE PLUS HUMAN GROWTH HORMONE POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS-SPECIFYING)
