U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 19:01:03 UTC 2023
Edited
by admin
on Sat Dec 16 19:01:03 UTC 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name SEROTYPE RH10
Part whole
Record UNII
8G4FJ7F8EY
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
LIXMABEGAGENE RELDUPARVOVEC
INN  
Official Name English
A RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE RH.10 (RAAVRH.10) VECTOR ENCODING HUMAN .BETA.-GALACTOSIDASE (GLB1), UNDER CONTROL OF THE SYNTHETIC CAG PROMOTER (CMV IMMEDIATE-EARLY ENHANCER/CHICKEN .BETA.-ACTIN (CB) PROMOTER, CHICKEN .BET
Common Name English
LYS-GM101
Code English
lixmabegagene relduparvovec [INN]
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR LYS-GM101 SYNTHETIC CAG PROMOTER PLUS HUMAN .BETA.-GALACTOSIDASE TRANSGENE PLUS HUMAN GROWTH HORMONE POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS-SPECIFYING)
Common Name English
Code System Code Type Description
INN
11919
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY
NCI_THESAURUS
C188537
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY
CAS
2461531-19-9
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY
FDA UNII
8G4FJ7F8EY
Created by admin on Sat Dec 16 19:01:04 UTC 2023 , Edited by admin on Sat Dec 16 19:01:04 UTC 2023
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR LIXMABEGAGENE RELDUPARVOVEC TRANSGENE INSERT Z38T3Q3D4G