U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
inlezifigene civaparvovec [INN]
Preferred Name English
INLEZIFIGENE CIVAPARVOVEC
INN  
Official Name English
A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV REP2-CAP6) VECTOR, EXPRESSING A CDNA THAT TARGETS 447-461 BP OF THE ALBUMIN LOCUS (RELATIVE TO THE TRANSCRIPTION INITIATION SITE), FUSED TO THE OBLIGATE HETERODIMERIC FOKI NUCLEASE DOMAI
Systematic Name English
Code System Code Type Description
SMS_ID
300000005923
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
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FDA UNII
87RN2MR2FP
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
CAS
2143578-31-6
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
INN
10977
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
NCI_THESAURUS
C175089
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY