U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 05:57:23 GMT 2025
Edited
by admin
on Wed Apr 02 05:57:23 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SUBSTRAIN
Infraspecific Name rAAV(Rep2-Cap6)-ApoE / hAAT-ZFP 47171-FokI-ELD vector
Part whole
Record UNII
87RN2MR2FP
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
inlezifigene civaparvovec [INN]
Preferred Name English
INLEZIFIGENE CIVAPARVOVEC
INN  
Official Name English
A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV REP2-CAP6) VECTOR, EXPRESSING A CDNA THAT TARGETS 447-461 BP OF THE ALBUMIN LOCUS (RELATIVE TO THE TRANSCRIPTION INITIATION SITE), FUSED TO THE OBLIGATE HETERODIMERIC FOKI NUCLEASE DOMAI
Systematic Name English
Code System Code Type Description
SMS_ID
300000005923
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
FDA UNII
87RN2MR2FP
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
CAS
2143578-31-6
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
INN
10977
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
NCI_THESAURUS
C175089
Created by admin on Wed Apr 02 05:57:23 GMT 2025 , Edited by admin on Wed Apr 02 05:57:23 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR INLEZIFIGENE CIVAPARVOVEC TRANSGENE INSERT ZR4A4C333T