U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
Zertomibgene Cazparvovec
INN  
Official Name English
DNA (recombinant replication-deficient adeno-associated virus 9 vector TN-201 synthetic cardiac-selective promoter plus human myosin-binding protein MYBPC3 transgene plus synthetic polyadenylation signal plus adeno-associated virus 2 inverted terminal re
Preferred Name English
zertomibgene cazparvovec [INN]
Common Name English
recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector, encoding myosin-binding protein C (MYBPC3), under control of a synthetic cardiomyocyte-specific cardiac troponin T2 (TNNT2) promoter (pCard1) and a synthetic polyadenylation s
Common Name English
Code System Code Type Description
SMS_ID
300000038205
Created by admin on Wed Apr 02 21:25:57 GMT 2025 , Edited by admin on Wed Apr 02 21:25:57 GMT 2025
PRIMARY
INN
13225
Created by admin on Wed Apr 02 21:25:57 GMT 2025 , Edited by admin on Wed Apr 02 21:25:57 GMT 2025
PRIMARY
CAS
2920655-43-0
Created by admin on Wed Apr 02 21:25:57 GMT 2025 , Edited by admin on Wed Apr 02 21:25:57 GMT 2025
PRIMARY
FDA UNII
64SQ6WC9ET
Created by admin on Wed Apr 02 21:25:57 GMT 2025 , Edited by admin on Wed Apr 02 21:25:57 GMT 2025
PRIMARY
NCI_THESAURUS
C211737
Created by admin on Wed Apr 02 21:25:57 GMT 2025 , Edited by admin on Wed Apr 02 21:25:57 GMT 2025
PRIMARY