U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
AT-GTX-501
Preferred Name English
SESICLENEGENE COSAPARVOVEC
INN  
Official Name English
sesiclenegene cosaparvovec [INN]
Common Name English
A NON-REPLICATING SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS (SCAAV) VECTOR ENCODING HUMAN CEROID-LIPOFUSCINOSIS NEURONAL PROTEIN 6. A RECOMBINANT NON-REPLICATING SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS SEROTYPE 9 (SCAAV9) VECTOR, ENCODING HUMAN CEROID-
Common Name English
DNA (SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS 9 VECTOR AT-GTX-501 HUMAN CYTOMEGALOVIRUS ENHANCER PLUS CHICKEN .BETA.-ACTIN HYBRID PROMOTER PLUS HUMAN CEROID-LIPOFUSCINOSIS NEURONAL PROTEIN CLN6-SPECIFYING)
Common Name English
Code System Code Type Description
INN
11600
Created by admin on Wed Apr 02 12:05:47 GMT 2025 , Edited by admin on Wed Apr 02 12:05:47 GMT 2025
PRIMARY INN
SMS_ID
100000183307
Created by admin on Wed Apr 02 12:05:47 GMT 2025 , Edited by admin on Wed Apr 02 12:05:47 GMT 2025
PRIMARY
CAS
2379806-98-9
Created by admin on Wed Apr 02 12:05:47 GMT 2025 , Edited by admin on Wed Apr 02 12:05:47 GMT 2025
PRIMARY
NCI_THESAURUS
C179119
Created by admin on Wed Apr 02 12:05:47 GMT 2025 , Edited by admin on Wed Apr 02 12:05:47 GMT 2025
PRIMARY
FDA UNII
53A6SJF4WE
Created by admin on Wed Apr 02 12:05:47 GMT 2025 , Edited by admin on Wed Apr 02 12:05:47 GMT 2025
PRIMARY