U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 18:42:45 UTC 2023
Edited
by admin
on Sat Dec 16 18:42:45 UTC 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SUBSTRAIN
Infraspecific Name scAAV9.CB.CLN6
Part whole
Record UNII
53A6SJF4WE
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
SESICLENEGENE COSAPARVOVEC
INN  
Official Name English
sesiclenegene cosaparvovec [INN]
Common Name English
AT-GTX-501
Code English
A NON-REPLICATING SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS (SCAAV) VECTOR ENCODING HUMAN CEROID-LIPOFUSCINOSIS NEURONAL PROTEIN 6. A RECOMBINANT NON-REPLICATING SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS SEROTYPE 9 (SCAAV9) VECTOR, ENCODING HUMAN CEROID-
Common Name English
DNA (SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS 9 VECTOR AT-GTX-501 HUMAN CYTOMEGALOVIRUS ENHANCER PLUS CHICKEN .BETA.-ACTIN HYBRID PROMOTER PLUS HUMAN CEROID-LIPOFUSCINOSIS NEURONAL PROTEIN CLN6-SPECIFYING)
Common Name English
Code System Code Type Description
INN
11600
Created by admin on Sat Dec 16 18:42:45 UTC 2023 , Edited by admin on Sat Dec 16 18:42:45 UTC 2023
PRIMARY INN
CAS
2379806-98-9
Created by admin on Sat Dec 16 18:42:45 UTC 2023 , Edited by admin on Sat Dec 16 18:42:45 UTC 2023
PRIMARY
NCI_THESAURUS
C179119
Created by admin on Sat Dec 16 18:42:45 UTC 2023 , Edited by admin on Sat Dec 16 18:42:45 UTC 2023
PRIMARY
FDA UNII
53A6SJF4WE
Created by admin on Sat Dec 16 18:42:45 UTC 2023 , Edited by admin on Sat Dec 16 18:42:45 UTC 2023
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY