U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
RANUZIFIGENE CIVAPARVOVEC
INN  
Official Name English
ranuzifigene civaparvovec [INN]
Preferred Name English
A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV REP2-CAP6) VECTOR, EXPRESSING A CDNA THAT TARGETS 468-485 BP OF THE ALBUMIN LOCUS (RELATIVE TO THE TRANSCRIPTION INITIATION SITE), FUSED TO THE OBLIGATE HETERODIMERIC FOKI NUCLEASE DOMAI
Systematic Name English
Code System Code Type Description
NCI_THESAURUS
C171801
Created by admin on Wed Apr 02 04:13:48 GMT 2025 , Edited by admin on Wed Apr 02 04:13:48 GMT 2025
PRIMARY
FDA UNII
52XT2AZD2N
Created by admin on Wed Apr 02 04:13:48 GMT 2025 , Edited by admin on Wed Apr 02 04:13:48 GMT 2025
PRIMARY
SMS_ID
300000005888
Created by admin on Wed Apr 02 04:13:48 GMT 2025 , Edited by admin on Wed Apr 02 04:13:48 GMT 2025
PRIMARY
INN
10980
Created by admin on Wed Apr 02 04:13:48 GMT 2025 , Edited by admin on Wed Apr 02 04:13:48 GMT 2025
PRIMARY
CAS
2143578-32-7
Created by admin on Wed Apr 02 04:13:48 GMT 2025 , Edited by admin on Wed Apr 02 04:13:48 GMT 2025
PRIMARY