U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
Renizgamglogene Autogedtemcel
INN   USAN  
Official Name English
EDIT 301
Preferred Name English
Autologous human CD34+ hematopoietic stem/precursor cells (HSPCs), obtained from peripheral blood by leukapheresis from plerixaformobilized sickle cell disease (SCD) patients or granulocyte colony stimulating factor (G-CSF) and plerixafor-mobilized trans
Common Name English
renizgamglogene autogedtemcel [INN]
Common Name English
EDIT-301 CD34+ hematopoietic stem cells
Common Name English
EDIT-301
Code English
RENIZGAMGLOGENE AUTOGEDTEMCEL [USAN]
Common Name English
Code System Code Type Description
INN
12733
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
SMS_ID
300000052161
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
NCI_THESAURUS
C203030
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
CAS
2923537-23-7
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
FDA UNII
4A4FLA6DZA
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
USAN
MN-162
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY