U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 17:23:39 GMT 2025
Edited
by admin
on Wed Apr 02 17:23:39 GMT 2025
Source Materials Class ORGANISM
Source Materials Type AUTOLOGOUS HUMAN
Source Materials State LIVE
Source Materials Parent
Part blood
Fraction Name cd34+ hematopoietic stem and progenitor cells (hspcs)
Record UNII
4A4FLA6DZA
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Renizgamglogene Autogedtemcel
INN   USAN  
Official Name English
EDIT 301
Preferred Name English
Autologous human CD34+ hematopoietic stem/precursor cells (HSPCs), obtained from peripheral blood by leukapheresis from plerixaformobilized sickle cell disease (SCD) patients or granulocyte colony stimulating factor (G-CSF) and plerixafor-mobilized trans
Common Name English
renizgamglogene autogedtemcel [INN]
Common Name English
EDIT-301 CD34+ hematopoietic stem cells
Common Name English
EDIT-301
Code English
RENIZGAMGLOGENE AUTOGEDTEMCEL [USAN]
Common Name English
Code System Code Type Description
INN
12733
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
SMS_ID
300000052161
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
NCI_THESAURUS
C203030
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
CAS
2923537-23-7
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
FDA UNII
4A4FLA6DZA
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
USAN
MN-162
Created by admin on Wed Apr 02 17:23:39 GMT 2025 , Edited by admin on Wed Apr 02 17:23:39 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY