U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
AZAMIDUGENE AUTOTEMCEL VECTOR
Common Name English
SELF-INACTIVATING LENTIVIRAL VECTOR EXPRESSING HUMAN ALPHA-L-IDURONIDASE (IDUA) UNDER THE CONTROL OF A HUMAN PHOSPHOGLYCERATE KINASE (PGK)PROMOTER THE CONSTRUCT IS FLANKED BY 5' AND 3' LONG TERMINAL REPEATS (LTRS) AND ALSO CONTAINS A HIV-1 .PSI. PACKAGIN
Preferred Name English
Code System Code Type Description
FDA UNII
2CX3CU3LQY
Created by admin on Wed Apr 02 12:56:47 GMT 2025 , Edited by admin on Wed Apr 02 12:56:47 GMT 2025
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