Search results for "ORPHAN DRUG|Designated/Approved|Treatment of alagille syndrome" in comments (approximate match)
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Class (Stereo):
CHEMICAL (ABSOLUTE)
Targets:
Maralixibat (Livmarli™) is a potent, apical, sodium‐dependent, bile acid transporter competitive inhibitor with minimal systemic absorption being developed by Mirum Pharmaceuticals for the treatment of rare cholestatic liver diseases including Alagil...