U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS
This repository is under review for potential modification in compliance with Administration directives.

Showing 1 - 3 of 3 results

Status:
Investigational

Class (Stereo):
CHEMICAL (ABSOLUTE)


Emixustat (formerly ACU-4429) is a nonretinoid compound with a unique mode of action in the retinal pigment epithelium, where it modulates the biosynthesis of visual chromophore through its effect on retinal pigment epithelium protein 65 (RPE65). Emi...
Status:
Possibly Marketed Outside US
First approved in 2024

Class (Stereo):
CHEMICAL (ACHIRAL)



Phenyl N-tert-butylnitrone (also known as α-Phenyl-N-tert-butylnitrone or PBN), a free radical spin trap, protects retinas against light-induced neurodegeneration by means of inhibition of RPE65 catalytic action. In addition, in experiments on rodent...
Status:
Investigational

Class (Stereo):
CHEMICAL (ABSOLUTE)


Emixustat (formerly ACU-4429) is a nonretinoid compound with a unique mode of action in the retinal pigment epithelium, where it modulates the biosynthesis of visual chromophore through its effect on retinal pigment epithelium protein 65 (RPE65). Emi...