U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 18:35:09 UTC 2023
Edited
by admin
on Sat Dec 16 18:35:09 UTC 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SEROTYPE
Infraspecific Name AAV9-GLB1 (AAV2 flanking-CBA-GLB1-SV40)
Part whole
Record UNII
ZMG9G56THB
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
BOMTABEGAGENE BAVOPARVOVEC
USAN   INN  
Official Name English
BOMTABEGAGENE BAVOPARVOVEC [USAN]
Common Name English
AAV9-GLB1
Code English
bomtabegagene bavoparvovec [INN]
Common Name English
AXO-AAV-GM1
Code English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS SEROTYPE 9 VECTOR AAV9-GLB1 CYTOMEGALOVIRUS IMMEDIATE EARLY ENHANCER FUSION WITH CHICKEN .BETA.-ACTIN PROMOTER/DONOR AND ACCEPTOR SPLICE SITE-CONTAINING INTRON/HUMAN LYSOSOMAL ACID .BETA.-GALACTOSIDASE TRANSGENE HG
Common Name English
Code System Code Type Description
USAN
HI-104
Created by admin on Sat Dec 16 18:35:09 UTC 2023 , Edited by admin on Sat Dec 16 18:35:09 UTC 2023
PRIMARY
CAS
2364477-20-1
Created by admin on Sat Dec 16 18:35:09 UTC 2023 , Edited by admin on Sat Dec 16 18:35:09 UTC 2023
PRIMARY
FDA UNII
ZMG9G56THB
Created by admin on Sat Dec 16 18:35:09 UTC 2023 , Edited by admin on Sat Dec 16 18:35:09 UTC 2023
PRIMARY
NCI_THESAURUS
C180640
Created by admin on Sat Dec 16 18:35:09 UTC 2023 , Edited by admin on Sat Dec 16 18:35:09 UTC 2023
PRIMARY
INN
11901
Created by admin on Sat Dec 16 18:35:09 UTC 2023 , Edited by admin on Sat Dec 16 18:35:09 UTC 2023
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR UNSPECIFIED SUBSTANCE
94c95d9b
(not in database)