U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Mon Mar 31 22:46:43 GMT 2025
Edited
by admin
on Mon Mar 31 22:46:43 GMT 2025
Sequence Type OLIGONUCLEOTIDE
Record UNII
ZE6EHM8Z3A
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
AD-51547
Preferred Name English
REVUSIRAN
INN   WHO-DD  
INN  
Official Name English
revusiran [INN]
Common Name English
Revusiran [WHO-DD]
Common Name English
Classification Tree Code System Code
FDA ORPHAN DRUG 477615
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
NCI_THESAURUS C307
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
Code System Code Type Description
NCI_THESAURUS
C152204
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
PRIMARY
EVMPD
SUB184392
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
PRIMARY
SMS_ID
100000170404
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
PRIMARY
CAS
1438322-82-7
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
PRIMARY
INN
9989
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
PRIMARY
FDA UNII
ZE6EHM8Z3A
Created by admin on Mon Mar 31 22:46:43 GMT 2025 , Edited by admin on Mon Mar 31 22:46:43 GMT 2025
PRIMARY
Sugar Site Range Site Count
2'-O-Methyl-Ribose 1_2;1_4;1_6;1_8;1_12;1_14-1_16;1_18;1_20;2_1;2_3;2_5;2_9;2_11-2_13;2_15;2_17;2_19;2_21;2_23 22 / 45
2'-Fluoro-Ribose 1_1;1_3;1_5;1_7;1_9-1_11;1_13;1_17;1_19;1_21-1_22;2_2;2_4;2_6-2_8;2_10;2_14;2_16;2_18;2_20;2_22 23 / 45
Linkage Site Range Site Count
Phosporothioate 2_22-2_23 2 / 43
Phosphate 1_2-1_22;2_2-2_21 41 / 43

Agent Modifications

Modification Process Modification Role Modification Type Amount Fragment Name Fragment ID

Physical Modifications

Modification Role Parameter Name Amount

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
NUCLEOTIDE SUBSTITUTION [1_22] 3'-TERMINUS CEMDISIRAN, TERMINAL SUGAR MODIFICATION- CQQ59545BV