Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 01:11:30 GMT 2025
by
admin
on
Wed Apr 02 01:11:30 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependoparvovirus |
| Organism Species | adeno-associated dependoparvovirus a |
| Infraspecific Type | RECOMBINANT VECTOR |
| Infraspecific Name | ADENO-ASSOCIATED VIRUS SEROTYPE 5 (AAV5) EXPRESSING THE PADUA VARIANT (R338L) OF HUMAN COAGULATION FACTOR IX |
| Part | whole |
| Record UNII |
Z5XCD5Q9RL
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Related Record | Type |
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| Name | Type | Language | ||
|---|---|---|---|---|
|
Official Name | English | ||
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Preferred Name | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Systematic Name | English | ||
|
Code | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
|
2156583-26-3
Created by
admin on Wed Apr 02 01:11:30 GMT 2025 , Edited by admin on Wed Apr 02 01:11:30 GMT 2025
|
PRIMARY | |||
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10963
Created by
admin on Wed Apr 02 01:11:30 GMT 2025 , Edited by admin on Wed Apr 02 01:11:30 GMT 2025
|
PRIMARY | |||
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Z5XCD5Q9RL
Created by
admin on Wed Apr 02 01:11:30 GMT 2025 , Edited by admin on Wed Apr 02 01:11:30 GMT 2025
|
PRIMARY | |||
|
C171798
Created by
admin on Wed Apr 02 01:11:30 GMT 2025 , Edited by admin on Wed Apr 02 01:11:30 GMT 2025
|
PRIMARY | |||
|
JK-202
Created by
admin on Wed Apr 02 01:11:30 GMT 2025 , Edited by admin on Wed Apr 02 01:11:30 GMT 2025
|
PRIMARY | |||
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300000005896
Created by
admin on Wed Apr 02 01:11:30 GMT 2025 , Edited by admin on Wed Apr 02 01:11:30 GMT 2025
|
PRIMARY | |||
|
Z5XCD5Q9RL
Created by
admin on Wed Apr 02 01:11:30 GMT 2025 , Edited by admin on Wed Apr 02 01:11:30 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
SUB_CONCEPT->SUBSTANCE |
|
||
|
TARGET->GENE REPLACEMENT |
|
||
|
EXPRESSED PROTEIN->VECTOR |
|
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
ACTIVE MOIETY |
|
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| INSERTED GENE EXPRESSION VECTOR | ETRANACOGENE DEZAPARVOVEC DNA INSERT | EI983WK411 |