U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name ADENO-ASSOCIATED VIRUS SEROTYPE 5 (AAV5) EXPRESSING THE PADUA VARIANT (R338L) OF HUMAN COAGULATION FACTOR IX
Part WHOLE
Record UNII
Z5XCD5Q9RL
Record Status Validated (UNII)
Record Version

Structural Modifications