U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 11:22:25 GMT 2025
Edited
by admin
on Wed Apr 02 11:22:25 GMT 2025
Nucleic Acid Type dsRNA
Sequence Origin SYNTHETIC
Sequence Type COMPLETE
Record UNII
YU6F4W95PG
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Lefelsiran Sodium
USAN  
Official Name English
DCR-1203
Preferred Name English
all-P-ambo-(3'?5')-2'-O-methyl-P-thioguanylyl-(3'?5')-2'-O-methyl-P-thioguanylyl-(3'?5')-2'-O-methyl-P-thiocytidylyl-(3'?5')-2'-O-methylcytidylyl-(3'?5')-2'-O-methyladenylyl-(3'?5')-2'-O-methylcytidylyl-(3'?5')-2'-O-methylcytidylyl-(3'?5')-2'-O-methyluri
Common Name English
DCR-A1203
Code English
LEFELSIRAN SODIUM [USAN]
Common Name English
RNA, ([4?-de(hydroxymethyl)-4?-[(hydroxymethoxyphosphinyl)methoxy]]Um-sp-(2?-deoxy-2?-fluoro)A-sp-(2?-deoxy-2?-fluoro)A-sp-(2?-deoxy-2?-fluoro)A-(2?-deoxy-2?-fluoro)C-Um-(2?-deoxy-2?-fluoro)G-Am-Gm-Um-Um-Um-Cm-(2?-deoxy-2?-fluoro)A-Um-Cm-Cm-Am-Cm-Cm-sp-G
Common Name English
Code System Code Type Description
CAS
2728713-54-8
Created by admin on Wed Apr 02 11:22:25 GMT 2025 , Edited by admin on Wed Apr 02 11:22:25 GMT 2025
PRIMARY
SMS_ID
300000027491
Created by admin on Wed Apr 02 11:22:25 GMT 2025 , Edited by admin on Wed Apr 02 11:22:25 GMT 2025
PRIMARY
USAN
KL-224
Created by admin on Wed Apr 02 11:22:25 GMT 2025 , Edited by admin on Wed Apr 02 11:22:25 GMT 2025
PRIMARY
FDA UNII
YU6F4W95PG
Created by admin on Wed Apr 02 11:22:25 GMT 2025 , Edited by admin on Wed Apr 02 11:22:25 GMT 2025
PRIMARY
NCI_THESAURUS
C203144
Created by admin on Wed Apr 02 11:22:25 GMT 2025 , Edited by admin on Wed Apr 02 11:22:25 GMT 2025
PRIMARY
Sugar Site Range Site Count
2'-O-Methyl-Ribose 1_1-1_7;1_12-1_36;2_1;2_6;2_8-2_13;2_15-2_22 48 / 58
2'-Fluoro-Ribose 1_8-1_11;2_2-2_5;2_7;2_14 10 / 58
Linkage Site Range Site Count
Sodium Phosporothioate 1_2;2_2-2_4;2_21-2_22 6 / 56
1_3-1_36;2_5-2_20 50 / 56
Related Record Type Details
ACTIVE MOIETY