Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 12:16:20 GMT 2025
by
admin
on
Wed Apr 02 12:16:20 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependoparvovirus |
| Organism Species | adeno-associated dependoparvovirus a |
| Infraspecific Type | RECOMBINANT VECTOR |
| Infraspecific Name | rAAV9/CMV/HEXB-P2A-HEXA |
| Part | whole |
| Record UNII |
XX923BN5NY
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
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Common Name | English | ||
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Preferred Name | English | ||
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Common Name | English | ||
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Common Name | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
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12045
Created by
admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
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PRIMARY | |||
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XX923BN5NY
Created by
admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
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PRIMARY | |||
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C188657
Created by
admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
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PRIMARY | |||
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2567881-77-8
Created by
admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
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PRIMARY | |||
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300000032081
Created by
admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
TARGET->ENZYME REPLACEMENT |
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||
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EXPRESSED PROTEIN->VECTOR |
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| Related Record | Type | Details | ||
|---|---|---|---|---|
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ACTIVE MOIETY |
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Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| INSERTED GENE EXPRESSION VECTOR | ENGABEXAGENE CINCESPARVOVEC TRANSGENE INSERT | RN9AXF4YZA |