U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 14:44:20 UTC 2023
Edited
by admin
on Sat Dec 16 14:44:20 UTC 2023
Nucleic Acid Type OLIGONUCLEOTIDE
Nucleic Acid Subtype
Sequence Type COMPLETE
Record UNII
X70RY8Q6LI
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
VUPANORSEN SODIUM
USAN  
Official Name English
VUPANORSEN SODIUM [USAN]
Common Name English
DNA, D((2'-O-(2-METHOXYETHYL))RG-SP-(2'-O-(2-METHOXYETHYL))RG-(2'-O-(2-METHOXYETHYL))RA-(2'-O-(2-METHOXYETHYL))M5RC-(2'-O-(2-METHOXYETHYL))RA-T-SP-T-SP-G-SP-M5C-SP-M5C-SP-A-SP-G-SP-T-SP-A-SP-A-SP-(2'-O-(2-METHOXYETHYL))M5RU-(2'-O-(2-METHOXYETHYL))M5RC-(2
Systematic Name English
AKCEA-ANGPTL3-LRX SODIUM
Code English
ISIS-703802 SODIUM
Code English
ISIS 703802 SODIUM
Code English
Code System Code Type Description
NCI_THESAURUS
C174943
Created by admin on Sat Dec 16 14:44:20 UTC 2023 , Edited by admin on Sat Dec 16 14:44:20 UTC 2023
PRIMARY
CAS
2172852-12-7
Created by admin on Sat Dec 16 14:44:20 UTC 2023 , Edited by admin on Sat Dec 16 14:44:20 UTC 2023
PRIMARY
FDA UNII
X70RY8Q6LI
Created by admin on Sat Dec 16 14:44:20 UTC 2023 , Edited by admin on Sat Dec 16 14:44:20 UTC 2023
PRIMARY
USAN
FG-168
Created by admin on Sat Dec 16 14:44:20 UTC 2023 , Edited by admin on Sat Dec 16 14:44:20 UTC 2023
PRIMARY
Sugar Site Range Site Count
2'-O-Methoxyethyl ribose 1_1-1_5;1_16-1_20 10 / 20
Deoxyribose (DNA) 1_6-1_15 10 / 20
Linkage Site Range Site Count
1_2-1_5;1_16-1_17 6 / 19
Sodium Phosporothioate 1_1;1_6-1_15;1_18-1_19 13 / 19
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
MOIETY RESIDUE_SPECIFIC Amount: SODIUM CATION LYR4M0NH37
NUCLEOSIDE_SUBSTITUTION [1_9] [1_10] SITE_SPECIFIC 5-METHYLDEOXYCYTIDINE B200GV71QM
NUCLEOSIDE_SUBSTITUTION [1_4] [1_17] [1_19] SITE_SPECIFIC 2'-O-(2-METHOXYETHYL)-5-METHYLCYTIDINE AOQ54IZZ6J
NUCLEOSIDE_SUBSTITUTION [1_1] 5'-TERMINUS UNSPECIFIED SUBSTANCE
91ce9173
(not in database)
Name Property Type Amount Referenced Substance Defining Parameters References
MOL_WEIGHT:NUMBER(CALCULATED) CHEMICAL