Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 04:10:09 GMT 2025
by
admin
on
Wed Apr 02 04:10:09 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependoparvovirus |
| Organism Species | adeno-associated dependoparvovirus a |
| Infraspecific Type | SUBSTRAIN |
| Infraspecific Name | rAAV2/2-ND4 vector |
| Part | whole |
| Record UNII |
X0R16875YD
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Official Name | English | ||
|
Preferred Name | English | ||
|
Common Name | English | ||
|
Common Name | English | ||
|
Code | English |
| Classification Tree | Code System | Code | ||
|---|---|---|---|---|
|
FDA ORPHAN DRUG |
412013
Created by
admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
|
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
|
300000011810
Created by
admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
|
PRIMARY | |||
|
X0R16875YD
Created by
admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
|
PRIMARY | |||
|
C174939
Created by
admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
|
PRIMARY | |||
|
10256
Created by
admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
|
PRIMARY | |||
|
1640969-63-6
Created by
admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
|
NO STRUCTURE GIVEN | |||
|
NCT02652767
Created by
admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
EXPRESSED PROTEIN->VECTOR |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
ACTIVE MOIETY |
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| INSERTED GENE EXPRESSION VECTOR | LENADOGENE NOLPARVOVEC TRANSGENE INSERT | ZW25T5E6XH |