U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 04:10:09 GMT 2025
Edited
by admin
on Wed Apr 02 04:10:09 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SUBSTRAIN
Infraspecific Name rAAV2/2-ND4 vector
Part whole
Record UNII
X0R16875YD
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
LENADOGENE NOLPARVOVEC
INN  
Official Name English
GS-010
Preferred Name English
Lenadogene nolparvovec [WHO-DD]
Common Name English
lenadogene nolparvovec [INN]
Common Name English
GS010
Code English
Classification Tree Code System Code
FDA ORPHAN DRUG 412013
Created by admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
Code System Code Type Description
SMS_ID
300000011810
Created by admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
PRIMARY
FDA UNII
X0R16875YD
Created by admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
PRIMARY
NCI_THESAURUS
C174939
Created by admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
PRIMARY
INN
10256
Created by admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
PRIMARY
CAS
1640969-63-6
Created by admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
NO STRUCTURE GIVEN
CLINICAL_TRIALS.GOV
NCT02652767
Created by admin on Wed Apr 02 04:10:09 GMT 2025 , Edited by admin on Wed Apr 02 04:10:09 GMT 2025
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR LENADOGENE NOLPARVOVEC TRANSGENE INSERT ZW25T5E6XH