U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 12:33:28 GMT 2025
Edited
by admin
on Wed Apr 02 12:33:28 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name AAV1.CB7.CI.hPGRN.rBG
Part whole
Record UNII
VF7KK47ENX
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Alnugranogene Aldeparvovec
INN  
Official Name English
DNA (recombinant replication-defective adeno-associated virus serotype 1 vector PBFT02 cytomegalovirus enhancer fusion with chicken ?-actin promoter plus chicken ?-actin intron plus human granulin precursor codon-optimized gene GRN plus rabbit ?-globin p
Preferred Name English
alnugranogene aldeparvovec [INN]
Common Name English
Code System Code Type Description
NCI_THESAURUS
C190489
Created by admin on Wed Apr 02 12:33:28 GMT 2025 , Edited by admin on Wed Apr 02 12:33:28 GMT 2025
PRIMARY
INN
12226
Created by admin on Wed Apr 02 12:33:28 GMT 2025 , Edited by admin on Wed Apr 02 12:33:28 GMT 2025
PRIMARY
FDA UNII
VF7KK47ENX
Created by admin on Wed Apr 02 12:33:28 GMT 2025 , Edited by admin on Wed Apr 02 12:33:28 GMT 2025
PRIMARY
CAS
2607030-08-8
Created by admin on Wed Apr 02 12:33:28 GMT 2025 , Edited by admin on Wed Apr 02 12:33:28 GMT 2025
PRIMARY
SMS_ID
300000050069
Created by admin on Wed Apr 02 12:33:28 GMT 2025 , Edited by admin on Wed Apr 02 12:33:28 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY